Gene therapy

A technique to stop children from inheriting mitochondrial diseases has the potential to backfire

When it comes to a devastating blood disorder, sometimes two wrongs make a right

Early attempts to tailor disease treatment to individuals based on their DNA have met with equivocal success, raising concerns about a push to scale up such efforts

Birds and bees are just the beginning for this animal-altering technology

Experiment confirms that targeting senescent cells could treat age-related diseases

But federal law may prevent regulators from approving the technique

An external magnet guided cells to repair arteries in mice

Researchers are developing molecular switches that can inactivate transplanted genes, paving the way for safer gene therapies. First up—better treatments for cancer

Scientists try to understand why some patients get better and others don't

The gene editing method called CRISPR is already used in the lab to insert and remove genome defects in animal embryos

Whenever one examines any area of scientific inquiry, there are two important things to understand: where the science is today, and where it may lead us in the future.

By tweaking the charges of brain cells, researchers alter early brain development, opening a door to healing mature brains or undoing genetic damage